Expert consensus on the off-label use of drugs for pediatric rare diseases in China (2025 edition)
Xiaolan Mo, Houliang Deng, Jinlian Yang, Jiale Li, Shan Ouyang, Feng Chen, Yanqin Cui, Xia Gao, Hua Jiang, Xiaojing Li, Li Liu, Jie Liu, Lin Qiu, Xiaoming Rong, Zhe Wen, Jiayi Wang, Ping Zeng, Wen Zhang, Xiaopeng Zhao, Juan Zhou, Jie Chen, Pan Chen, Wenying Chen, Zebin Chen, Rui Fang, Xiaomei Fan, Y · 2025
Read Expert consensus on the off-label use of drugs for pediatric rare diseases in China (2025 edition) by Xiaolan Mo, Houliang Deng, Jinlian Yang, Jiale Li, Shan Ouyang, Feng Chen, Yanqin Cui, Xia Gao, Hua Jiang, Xiaojing Li, Li Liu, Jie Liu, Lin Qiu, Xiaoming Rong, Zhe Wen, Jiayi Wang, Ping Zeng, Wen Zhang, Xiaopeng Zhao, Juan Zhou, Jie Chen, Pan Chen, Wenying Chen, Zebin Chen, Rui Fang, Xiaomei Fan, Y (2025) in the Tower of Babel, a free online library of public-domain works preserved in clean, searchable text. No sign-up. The full text is served as a plain-text file at a predictable URL, where text is present: https://antarctic-labs.com/tower-of-babel/pmc-12683492.txt.
Description
BackgroundThe package insert is a key reference and legal basis for clinical medication. However, in the field of rare diseases, advances in diagnosis and treatment often outpace updates to drug labels, resulting in widespread off-label drug use—a practice that is particularly common and often unavoidable in pediatric populations. Inappropriate off-label use, however, carries significant clinical and safety risks.
Catalog record
| CREATOR | Xiaolan Mo, Houliang Deng, Jinlian Yang, Jiale Li, Shan Ouyang, Feng Chen, Yanqin Cui, Xia Gao, Hua Jiang, Xiaojing Li, Li Liu, Jie Liu, Lin Qiu, Xiaoming Rong, Zhe Wen, Jiayi Wang, Ping Zeng, Wen Zhang, Xiaopeng Zhao, Juan Zhou, Jie Chen, Pan Chen, Wenying Chen, Zebin Chen, Rui Fang, Xiaomei Fan, Y |
|---|---|
| YEAR | 2025 |
| COLLECTION | PAPERS |
| FORMAT | TXT |
| FILE SIZE | 92 KB |
| VERSION | 1.0 |
| LICENSE | CC BY 4.0 |
| RIGHTS | CC BY |
| SOURCE | Europe PMC |